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Genie Replacement Motor

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SMA Therapeutics (4acd6a_b94333b61aa3469d9975be9998bf32c2.pdf)

544 KBBhavya Ravi, Michelle Harran Chan-Cortés, Charlotte J. SumnerEN 17 pages
Spinal muscular atrophy (SMA) has seen significant progress with three FDA-approved treatments: nusinersen, onasemnogene abeparvovec, and risdiplam, which...

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therapeutics spinal muscular atrophy progress three approved treatments nusinersen onasemnogene abeparvovec risdiplam which

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