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Myotonic Dystrophy Report.pdf

MDFVoicePatientReportMay2017.pdf
Preview of Myotonic Dystrophy Report
🔗 Source: myotonic.org
📊 Size: 8.25 MB
📄 Pages: 161 pages
⬇️ Downloads: 53

Summary

Myotonic Dystrophy Externally-Led Patient-Focused Drug Development meeting was held on September 15, 2016, hosted by the Myotonic Dystrophy Foundation, to capture the voice of patients and caregivers, and elicit perspectives on the disease, as part of the FDA's Patient-Focused Drug Development Initiative. The meeting discussed the clinical characteristics of Myotonic Dystrophy Type 1 (DM1) and Type 2 (DM2), including symptoms, treatment, and quality of life, with the goal of informing regulatory decision-making and expanding the benefits of the FDA's initiative.

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Description

Myotonic Dystrophy Externally-Led Patient-Focused Drug Development meeting was held on September 15, 2016, hosted by the Myotonic Dystrophy Foundation, to...

Technical Information

  • File Format: PDF
  • File Size: 8.25 MB
  • Pages: 161
  • Language: EN
  • Total Downloads: 53
  • Last Updated: 1 week ago

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